Accelerate RARE Working Groups
Monday, September 14, 2026
Objectives:
Develop stakeholder consensus on rare disease–specific clinical development topics.
Create briefing documents, guidelines and white papers to meaningfully accelerate rare disease clinical development.
Topic Proposals:
Please feel free to propose a meaningful 2026 workshop topic by sending an email to miro@raretrialssummit.com.
2025 Report:
37 experts from biopharma and patient advocacy convened at the 2025 Summit to draft the priorities of the rare disease clinical development community ahead of the upcoming PDUFA VIII reauthorization.
