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2026 Rare Trials Summit
2026 Rare Trials Summit
2026 Agenda
Register
Speak
Exhibit
Venue
Accelerate RARE
2025 Videos
Login Account
2026 Agenda
Register
Speak
Exhibit
Venue
Accelerate RARE
2025 Videos
Login Account

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  • Closing Panel,
• 9/22/25

Closing Panel: Beyond “One Disease At a Time”: Platform Approaches to Accelerate Gene Therapy Trials

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Case Studies in Rare Disease Commercialization: Lessons Learned

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