Patient Advocacy Community

Patient advocacy organizations are essential partners in accelerating rare disease therapy development.

The Rare Trials Summit is proud to welcome leading patient advocacy organizations that are helping shape clinical trial design, patient identification, regulatory policy, endpoint development, and long-term patient support.

Why Meet Our Patient Advocacy Partners?

Patient advocacy organizations can help sponsors:

• Identify and educate patients earlier

• Improve protocol design and endpoint selection

• Support recruitment and long-term retention

• Develop natural history studies and registries

• Inform FDA and payer engagement

• Build sustainable patient support programs