Closing Panel, • 9/22/25 Closing Panel: Beyond “One Disease At a Time”: Platform Approaches to Accelerate Gene Therapy Trials You Might Also Like Innovating Clinical Outcome Assessments in Rare Disease Trials: Integrating Patient-Centered Measures and Digital Health Technologies Aligning Trials with Patient-Lived Experiences Beyond the Feasibility Survey: Strategic Site Selection to Accelerate Trials and Optimize Resources Beyond Biotech: The Rise of Nontraditional Sponsors in Rare Disease Trials What Matters to Payers: Conversations You Should Start During Phase 2
Closing Panel, • 9/22/25 Closing Panel: Beyond “One Disease At a Time”: Platform Approaches to Accelerate Gene Therapy Trials You Might Also Like Innovating Clinical Outcome Assessments in Rare Disease Trials: Integrating Patient-Centered Measures and Digital Health Technologies Aligning Trials with Patient-Lived Experiences Beyond the Feasibility Survey: Strategic Site Selection to Accelerate Trials and Optimize Resources Beyond Biotech: The Rise of Nontraditional Sponsors in Rare Disease Trials What Matters to Payers: Conversations You Should Start During Phase 2
