Sign up to view this video Join Now Closing Panel, • 9/22/25 Closing Panel: Beyond “One Disease At a Time”: Platform Approaches to Accelerate Gene Therapy Trials You Might Also Like Case Studies in Rare Disease Commercialization: Lessons Learned Designing Trials with the End in Mind: Building Market Access into Rare Disease Clinical Development Patient Recruitment and Engagement in in Global, Multisite Rare Disease Trials Patient-Centric Commercialization: Integrating Patient Voices into Market Access Strategies Reducing Patient Burden in Rare Disease Trials
Sign up to view this video Join Now Closing Panel, • 9/22/25 Closing Panel: Beyond “One Disease At a Time”: Platform Approaches to Accelerate Gene Therapy Trials You Might Also Like Case Studies in Rare Disease Commercialization: Lessons Learned Designing Trials with the End in Mind: Building Market Access into Rare Disease Clinical Development Patient Recruitment and Engagement in in Global, Multisite Rare Disease Trials Patient-Centric Commercialization: Integrating Patient Voices into Market Access Strategies Reducing Patient Burden in Rare Disease Trials