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2026 Rare Trials Summit
2026 Rare Trials Summit
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2026 Rare Trials Summit
2026 Rare Trials Summit
2026 Agenda
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Advocacy
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2026 Agenda
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Advocacy
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  • Patient Voice,
• 9/19/25

Decentralized by Design: Operationalizing Hybrid Rare Disease Trials

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How to Accelerate the Adoption of Decentralized Trials for Rare Disease Indications

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Beyond Biotech: The Rise of Nontraditional Sponsors in Rare Disease Trials

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