Sign up to view this video Join Now Trial Design, • 9/22/25 Innovating Clinical Outcome Assessments in Rare Disease Trials: Integrating Patient-Centered Measures and Digital Health Technologies Previous Operationalizing Precision Medicine in Rare Disease Trials You Might Also Like Leveraging Patient Advocacy To Scale Rare Disease Trials Operationalizing Precision Medicine in Rare Disease Trials Decentralized by Design: Operationalizing Hybrid Rare Disease Trials Case Studies in Rare Disease Commercialization: Lessons Learned Rare Isn’t Small: Incorporating Operational Excellence into Global, Multisite Rare Disease Trials
Sign up to view this video Join Now Trial Design, • 9/22/25 Innovating Clinical Outcome Assessments in Rare Disease Trials: Integrating Patient-Centered Measures and Digital Health Technologies Previous Operationalizing Precision Medicine in Rare Disease Trials You Might Also Like Leveraging Patient Advocacy To Scale Rare Disease Trials Operationalizing Precision Medicine in Rare Disease Trials Decentralized by Design: Operationalizing Hybrid Rare Disease Trials Case Studies in Rare Disease Commercialization: Lessons Learned Rare Isn’t Small: Incorporating Operational Excellence into Global, Multisite Rare Disease Trials