Opening Keynotes, • 9/22/25 Opening Keynote: The Evolving Regulatory Environment for Rare Disease Trials Next Opening Keynote: The Future of Rare Disease Trials You Might Also Like Beyond Biotech: The Rise of Nontraditional Sponsors in Rare Disease Trials Optimizing Rare Disease Clinical Trials with Real World Data Using NLP & AI Closing Panel: Beyond “One Disease At a Time”: Platform Approaches to Accelerate Gene Therapy Trials Accelerating Rare Disease Therapies: Strategies for Efficient Clinical Development Solutions for Trial Design Challenges in Rare Disease Trials
Opening Keynotes, • 9/22/25 Opening Keynote: The Evolving Regulatory Environment for Rare Disease Trials Next Opening Keynote: The Future of Rare Disease Trials You Might Also Like Beyond Biotech: The Rise of Nontraditional Sponsors in Rare Disease Trials Optimizing Rare Disease Clinical Trials with Real World Data Using NLP & AI Closing Panel: Beyond “One Disease At a Time”: Platform Approaches to Accelerate Gene Therapy Trials Accelerating Rare Disease Therapies: Strategies for Efficient Clinical Development Solutions for Trial Design Challenges in Rare Disease Trials
