Sign up to view this video Join Now Opening Keynotes, • 9/22/25 Opening Keynote: The Evolving Regulatory Environment for Rare Disease Trials Next Opening Keynote: The Future of Rare Disease Trials You Might Also Like Reducing Patient Burden in Rare Disease Trials Innovating Clinical Outcome Assessments in Rare Disease Trials: Integrating Patient-Centered Measures and Digital Health Technologies Optimizing CRO and Vendor Selection - Examples from the Field Rare Isn’t Small: Incorporating Operational Excellence into Global, Multisite Rare Disease Trials Purpose-Driven Metrics: Running Gene Therapy Trials with KPIs That Matter
Sign up to view this video Join Now Opening Keynotes, • 9/22/25 Opening Keynote: The Evolving Regulatory Environment for Rare Disease Trials Next Opening Keynote: The Future of Rare Disease Trials You Might Also Like Reducing Patient Burden in Rare Disease Trials Innovating Clinical Outcome Assessments in Rare Disease Trials: Integrating Patient-Centered Measures and Digital Health Technologies Optimizing CRO and Vendor Selection - Examples from the Field Rare Isn’t Small: Incorporating Operational Excellence into Global, Multisite Rare Disease Trials Purpose-Driven Metrics: Running Gene Therapy Trials with KPIs That Matter
