0
Skip to Content
2026 Rare Trials Summit
2026 Rare Trials Summit
2026 Agenda
Register
Speak
Exhibit
Venue
Accelerate RARE
2025 Videos
Login Account
2026 Rare Trials Summit
2026 Rare Trials Summit
2026 Agenda
Register
Speak
Exhibit
Venue
Accelerate RARE
2025 Videos
Login Account
2026 Agenda
Register
Speak
Exhibit
Venue
Accelerate RARE
2025 Videos
Login Account

Sign up to view this video

Join Now
  • Trial Design,
• 9/22/25

Accelerating Rare Disease Therapies: Strategies for Efficient Clinical Development

Previous

Opening Keynote: The Future of Rare Disease Trials

Next

Adaptive & Precision-Driven Trials: Platform and MATCH Models for Rare Disease Breakthroughs

You Might Also Like

Related Video Item Thumbnail Opening Keynote: The Future of Rare Disease Trials
Related Video Item Thumbnail Ethics and Strategies for Returning Individual Patient Data Collected in Clinical Research
Related Video Item Thumbnail Closing Panel: Beyond “One Disease At a Time”: Platform Approaches to Accelerate Gene Therapy Trials
Related Video Item Thumbnail Innovating Clinical Outcome Assessments in Rare Disease Trials: Integrating Patient-Centered Measures and Digital Health Technologies
Related Video Item Thumbnail Beyond the Feasibility Survey: Strategic Site Selection to Accelerate Trials and Optimize Resources

© 2025 Rare Trials Summit. All rights reserved.