Sign up to view this video Join Now Trial Design, • 9/22/25 Accelerating Rare Disease Therapies: Strategies for Efficient Clinical Development Previous Opening Keynote: The Future of Rare Disease Trials Next Adaptive & Precision-Driven Trials: Platform and MATCH Models for Rare Disease Breakthroughs You Might Also Like Opening Keynote: The Future of Rare Disease Trials Ethics and Strategies for Returning Individual Patient Data Collected in Clinical Research Closing Panel: Beyond “One Disease At a Time”: Platform Approaches to Accelerate Gene Therapy Trials Innovating Clinical Outcome Assessments in Rare Disease Trials: Integrating Patient-Centered Measures and Digital Health Technologies Beyond the Feasibility Survey: Strategic Site Selection to Accelerate Trials and Optimize Resources
Sign up to view this video Join Now Trial Design, • 9/22/25 Accelerating Rare Disease Therapies: Strategies for Efficient Clinical Development Previous Opening Keynote: The Future of Rare Disease Trials Next Adaptive & Precision-Driven Trials: Platform and MATCH Models for Rare Disease Breakthroughs You Might Also Like Opening Keynote: The Future of Rare Disease Trials Ethics and Strategies for Returning Individual Patient Data Collected in Clinical Research Closing Panel: Beyond “One Disease At a Time”: Platform Approaches to Accelerate Gene Therapy Trials Innovating Clinical Outcome Assessments in Rare Disease Trials: Integrating Patient-Centered Measures and Digital Health Technologies Beyond the Feasibility Survey: Strategic Site Selection to Accelerate Trials and Optimize Resources