Trial Design, • 9/22/25 Accelerating Rare Disease Therapies: Strategies for Efficient Clinical Development Previous Opening Keynote: The Future of Rare Disease Trials Next Adaptive & Precision-Driven Trials: Platform and MATCH Models for Rare Disease Breakthroughs You Might Also Like Ethics and Strategies for Returning Individual Patient Data Collected in Clinical Research Opening Keynote: The Evolving Regulatory Environment for Rare Disease Trials Beyond the Feasibility Survey: Strategic Site Selection to Accelerate Trials and Optimize Resources Rare Isn’t Small: Incorporating Operational Excellence into Global, Multisite Rare Disease Trials What Matters to Payers: Conversations You Should Start During Phase 2
Trial Design, • 9/22/25 Accelerating Rare Disease Therapies: Strategies for Efficient Clinical Development Previous Opening Keynote: The Future of Rare Disease Trials Next Adaptive & Precision-Driven Trials: Platform and MATCH Models for Rare Disease Breakthroughs You Might Also Like Ethics and Strategies for Returning Individual Patient Data Collected in Clinical Research Opening Keynote: The Evolving Regulatory Environment for Rare Disease Trials Beyond the Feasibility Survey: Strategic Site Selection to Accelerate Trials and Optimize Resources Rare Isn’t Small: Incorporating Operational Excellence into Global, Multisite Rare Disease Trials What Matters to Payers: Conversations You Should Start During Phase 2
