Sign up to view this video Join Now Patient Voice, • 9/19/25 Leveraging Patient Advocacy To Scale Rare Disease Trials Previous Beyond Biotech: The Rise of Nontraditional Sponsors in Rare Disease Trials Next How To Prevent Failure in Rare Disease Trials? You Might Also Like Optimizing CRO and Vendor Selection - Examples from the Field Opening Keynote: The Future of Rare Disease Trials Innovating Clinical Outcome Assessments in Rare Disease Trials: Integrating Patient-Centered Measures and Digital Health Technologies Case Studies in Rare Disease Commercialization: Lessons Learned Patient Recruitment and Engagement in in Global, Multisite Rare Disease Trials
Sign up to view this video Join Now Patient Voice, • 9/19/25 Leveraging Patient Advocacy To Scale Rare Disease Trials Previous Beyond Biotech: The Rise of Nontraditional Sponsors in Rare Disease Trials Next How To Prevent Failure in Rare Disease Trials? You Might Also Like Optimizing CRO and Vendor Selection - Examples from the Field Opening Keynote: The Future of Rare Disease Trials Innovating Clinical Outcome Assessments in Rare Disease Trials: Integrating Patient-Centered Measures and Digital Health Technologies Case Studies in Rare Disease Commercialization: Lessons Learned Patient Recruitment and Engagement in in Global, Multisite Rare Disease Trials