11/7/26 From Data to Discovery: Finding the Right Patients Across the Therapy Lifecycle Previous OPENING KEYNOTE - From Breakthrough to Access: How Advocacy and Policy Decide What Reaches Patients. Next From Awareness to Activation - Converting Rare Patient Identification into Trial Enrollment You Might Also Like Learning More from Less: Smarter Design and Execution in Rare Disease Trials Accelerated Pathways and Global Harmonization Mock Formal FDA Meeting: How to Respond When FDA Disagrees Bridging the Generational Divide in Rare Disease Clinical Trials: Tailoring Communication to Maximize Recruitment, Retention, and Equity Retention by Design - Keeping Families Engaged for Multi-Year Studies
11/7/26 From Data to Discovery: Finding the Right Patients Across the Therapy Lifecycle Previous OPENING KEYNOTE - From Breakthrough to Access: How Advocacy and Policy Decide What Reaches Patients. Next From Awareness to Activation - Converting Rare Patient Identification into Trial Enrollment You Might Also Like Learning More from Less: Smarter Design and Execution in Rare Disease Trials Accelerated Pathways and Global Harmonization Mock Formal FDA Meeting: How to Respond When FDA Disagrees Bridging the Generational Divide in Rare Disease Clinical Trials: Tailoring Communication to Maximize Recruitment, Retention, and Equity Retention by Design - Keeping Families Engaged for Multi-Year Studies
