11/8/26 OPENING KEYNOTE - From Breakthrough to Access: How Advocacy and Policy Decide What Reaches Patients. Next From Data to Discovery: Finding the Right Patients Across the Therapy Lifecycle You Might Also Like Mock Formal FDA Meeting: How to Respond When FDA Disagrees Mapping the Rare Patient Journey Write Your Own Endpoint Justification Modeling Value Across the Rare Disease Patient Journey From Data to Discovery: Finding the Right Patients Across the Therapy Lifecycle
11/8/26 OPENING KEYNOTE - From Breakthrough to Access: How Advocacy and Policy Decide What Reaches Patients. Next From Data to Discovery: Finding the Right Patients Across the Therapy Lifecycle You Might Also Like Mock Formal FDA Meeting: How to Respond When FDA Disagrees Mapping the Rare Patient Journey Write Your Own Endpoint Justification Modeling Value Across the Rare Disease Patient Journey From Data to Discovery: Finding the Right Patients Across the Therapy Lifecycle
