Innovating Clinical Outcome Assessments in Rare Disease Trials: Integrating Patient-Centered Measures and Digital Health Technologies — 2026 Rare Trials Summit

Trial Design

• 9/22/25

Innovating Clinical Outcome Assessments in Rare Disease Trials: Integrating Patient-Centered Measures and Digital Health Technologies

Operationalizing Precision Medicine in Rare Disease Trials

Reducing Patient Burden in Rare Disease Trials