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2026 Agenda
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Exhibit
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2025 Videos
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2026 Agenda
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2025 Videos
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  • Trial Design,
• 9/25/25

Operationalizing Precision Medicine in Rare Disease Trials

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AI-Driven Patient Identification and Recruitment

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Innovating Clinical Outcome Assessments in Rare Disease Trials: Integrating Patient-Centered Measures and Digital Health Technologies

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