11/8/26 OPENING KEYNOTE - From Breakthrough to Access: How Advocacy and Policy Decide What Reaches Patients. Next From Data to Discovery: Finding the Right Patients Across the Therapy Lifecycle You Might Also Like One Shot, No Slack: The Clinical Decisions That Make or Break a Rare Disease Program From Data to Discovery: Finding the Right Patients Across the Therapy Lifecycle Practical Application of Bayesian Networks in Rare Disease Trials Leveraging Natural History and RWE for Rare Approvals Platform and Basket Trials in Rare Disease: What’s Working, What Isn’t, and What It Takes to Scale
11/8/26 OPENING KEYNOTE - From Breakthrough to Access: How Advocacy and Policy Decide What Reaches Patients. Next From Data to Discovery: Finding the Right Patients Across the Therapy Lifecycle You Might Also Like One Shot, No Slack: The Clinical Decisions That Make or Break a Rare Disease Program From Data to Discovery: Finding the Right Patients Across the Therapy Lifecycle Practical Application of Bayesian Networks in Rare Disease Trials Leveraging Natural History and RWE for Rare Approvals Platform and Basket Trials in Rare Disease: What’s Working, What Isn’t, and What It Takes to Scale
