Patient Voice, • 9/19/25 Reducing Patient Burden in Rare Disease Trials Next Ethics and Strategies for Returning Individual Patient Data Collected in Clinical Research You Might Also Like Aligning Trials with Patient-Lived Experiences Opening Keynote: The Evolving Regulatory Environment for Rare Disease Trials What Matters to Payers: Conversations You Should Start During Phase 2 Rare Isn’t Small: Incorporating Operational Excellence into Global, Multisite Rare Disease Trials Closing Panel: Beyond “One Disease At a Time”: Platform Approaches to Accelerate Gene Therapy Trials
Patient Voice, • 9/19/25 Reducing Patient Burden in Rare Disease Trials Next Ethics and Strategies for Returning Individual Patient Data Collected in Clinical Research You Might Also Like Aligning Trials with Patient-Lived Experiences Opening Keynote: The Evolving Regulatory Environment for Rare Disease Trials What Matters to Payers: Conversations You Should Start During Phase 2 Rare Isn’t Small: Incorporating Operational Excellence into Global, Multisite Rare Disease Trials Closing Panel: Beyond “One Disease At a Time”: Platform Approaches to Accelerate Gene Therapy Trials
